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Sarepta touts three-year Duchenne gene therapy data after patient deaths

Sarepta said the effects of its Duchenne muscular dystrophy gene therapy were durable three years after treatment, based on longer-term findings from patients in its key clinical trial.

This report was first published by Endpoints News. To see the original version, click here

Sarepta said the effects of its Duchenne muscular dystrophy gene therapy were durable three years after treatment, based on longer-term findings from patients in its key clinical trial.

The data come after a tumultuous year for Sarepta and its gene therapy Elevidys, in which there were two patient deaths due to the one-time treatment.

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