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Beam Therapeutics has provided a much-awaited update on its therapy that uses a form of CRISPR called base editing to precisely fix a single genetic typo responsible for a rare genetic disease.
Beam Therapeutics发布了备受期待的最新进展:其疗法采用一种名为“碱基编辑”的CRISPR技术,能够精确修复导致一种罕见遗传病的单个基因“错别字”。
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